None
EN
STAT+: Skylark Bio kicks off new gene therapy trial for deafness
['O. Rose Broderick', 'Rose Covers Disability', 'Mental Health', 'She Helps Write Stat S Daily', 'Disability In Health Care Reporting Fellow', 'Angus Chen', 'Adam Feuerstein', 'Allison Deangelis', 'Meghana Keshavan', 'Jason Mast']
STAT
Rose covers disability and mental health, and she helps write STAT’s daily Morning Rounds newsletter .
Confidential tips can be sent to Rose on Signal at rosebroderick.11.
Two years ago, scientists made history with a gene therapy that restored hearing for a small group of children who had been born deaf, allowing some of them to hear for the first time.
The robust gains and lack of safety concerns led the Food and Drug Administration to approve Regeneron’s Otarmeni therapy in April for the small group of people with this rare genetic mutation.
AdvertisementScientists are now eyeing other hearing-loss targets, including the holy grail — the GJB2 gene.